uniQure NV
Uniqure NV is a company based in the Netherlands specialized in gene therapy. It seeks to develop one-time administered treatments with potentially curative results for patients suffering from genetic and other devastating diseases. It develops, both internally and through partnerships, a pipeline of gene therapies. It produces adeno-associated virus based, or AAV-based, gene therapies in its own facilities with a proprietary, commercial-scale, current good manufacturing practices, compliant, manufacturing process. AMT-061, the Company’s lead product candidate for patients with hemophilia B, is going through a dosing phase of a pivotal study. AMT-130, the product candidate for patients with Huntington’s disease is in Phase I/II clinical study.
Stock Performance Snapshot
Analyst Rating
Analysts suggest buying uniQure's stock with a target price of $35.42, indicating good growth potential.
Financial Health
uniQure NV is performing well with strong revenue and cash flow, indicating healthy financial stability.
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Explore BasketWhy You’ll Want to Watch This Stock
Gene‑therapy focus
uniQure's core expertise is in AAV‑based gene therapy, which promises durable effects; however, clinical and manufacturing hurdles mean outcomes can vary.
Rare disease market
Targeting haemophilia and other rare conditions offers high unmet need and potential value, yet commercial uptake depends on pricing, reimbursement and long‑term data.
Regulatory milestones
Trial readouts and approval decisions drive valuation swings; these catalysts can create opportunities but also pose binary risks for investors.
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