Neoleukin Therapeutics, Inc.
Neurogene Inc. is a clinical-stage biotechnology company. The Company, through its proprietary transgene regulation technology, Expression Attenuation via Construct Tuning (EXACT), is building a product portfolio of genetic medicines for rare neurological diseases with high unmet needs not otherwise addressable by conventional gene therapy. Its clinical-stage program, NGN-401, utilize the EXACT platform, which is in development for the treatment of Rett syndrome, a disease with a patient population that has a significant unmet need, and that ultimately progresses to substantial neurological and physical impairment and premature death. NGN-401 is being evaluated in female patients with Rett syndrome in a Phase 1/2 open-label, multi-center clinical trial that assesses the safety, tolerability, and efficacy of two doses of NGN-401 delivered using a one-time intracerebral ventricular (ICV) procedure. It is also developing NGN-101 for the treatment of CLN5 Batten disease.
Stock Performance Snapshot
Analyst Rating
Analysts strongly recommend buying Neoleukin Therapeutics' stock, with a target price of $46.75.
Financial Health
Neoleukin Therapeutics is showing strong financial performance with healthy cash flow and book value.
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Explore BasketWhy You’ll Want to Watch This Stock
De novo protein design
Neoleukin’s engineered proteins aim to replicate immune signalling with potential safety benefits, though clinical proof is still evolving and outcomes are uncertain.
Data‑driven moves
Share direction often follows clinical readouts and regulatory news; trial results can create sharp moves in either direction.
Watch funding and partners
Cash runway and collaborations shape long‑term prospects; small‑cap biotech financing needs can dilute shareholders if additional capital is required.
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